While the precise mode of action of ganaxolone is yet unknown, it is believed to increase the activity of the neurotransmitter GABA (gamma-aminobutyric acid), which oversees reducing brain nerve activity. This causes the brain to calm down, which can lessen anxiety and stop seizures.
In preclinical and clinical research, ganaxolone has demonstrated efficacy for a variety of illnesses across its spectrum, including:
Patients with various kinds of epilepsy, including those with the illness that is treatment-resistant, have proven that ganaxolone is beneficial in lowering the frequency of their seizures.
A potential treatment for postpartum depression, which affects some women after giving birth. ganaxolone is also being investigated as a potential therapy for this genetic disorder, which produces symptoms like intellectual incapacity, behavioural issues, and emotional issues.